REGENXBIO Inc. (RGNX)
REGENXBIO Inc., a clinical-stage biotechnology company, provides gene therapy product candidates to deliver genes to cells to address genetic defects or to enable cells in the body to produce therapeutic proteins or antibodies that are intended to impact disease. Its gene therapy product candidates are based on NAV Technology Platform, a proprietary adeno-associated virus gene delivery platform. The company's lead product candidate is RGX-314, which is in Phase III clinical trial for the treatment of wet age-related macular degeneration. It is also developing RGX-121 that is in Phase I/II clinical trial to treat mucopolysaccharidosis type II;RGX-111, which is in Phase I/II clinical trial for treating mucopolysaccharidosis type I;RGX-181 which is in pre clinic stage for the treatment of late-infantile neuronal ceroid lipofuscinosis type II disease;RGX-202, to treat Duchenne muscular dystrophy which is in phase I/II clinical trial; and RGX-381, to treat the ocular manifestations of CLN2 disease which is in preclinical stage. REGENXBIO Inc. also licenses its NAV Technology Platform to other biotechnology and pharmaceutical companies; and has a collaboration and license agreement with Neurimmune AG to develop novel gene therapies. REGENXBIO Inc. was founded in 2008 and is headquartered in Rockville, Maryland.
$629.65M
Mr. Kenneth T. Mills
372.00
Rockville, MD
Sep 17, 2015
-2.43
$-5.24
0.58
3.21
-290.67%
-3.07
2.13
9.02
2.93
-41.30%
-57.79%
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iShares Core S&P Small-Cap ETF
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iShares S&P Small-Cap 600 Value ETF
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ETF Exposure (69)
Global X Genomics & Biotechnology ETF
GNOM
0.9%
Invesco S&P SmallCap Health Care ETF
PSCH
0.385%
SPDR S&P Biotech ETF
XBI
0.164055%
Direxion Daily S&P Biotech Bull 3X Shares
LABU
0.1150210664%
SPDR S&P Kensho New Economies Composite ETF
KOMP
0.089704%
Vanguard Strategic Small-Cap Equity Fund Investor Shares
VSTCX
0.08%
BlackRock Future Health ETF
BMED
0.06426%
Invesco Nasdaq Biotechnology ETF
IBBQ
0.057%
Vanguard S&P Small-Cap 600 Index Fund
VIOO
0.05%
Vanguard S&P Small-Cap 600 Value Index Fund
VIOV
0.05%
Vanguard Tax Managed Small Cap Fund
VTMSX
0.05%
Vanguard Tax-Managed Small-Cap Fund Institutional Shares
VTSIX
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Vanguard Russell 2000 Value Index Fund
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iShares Biotechnology ETF
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SPDR S&P 600 Small Cap Value ETF
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ProShares UltraPro Russell2000
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ProShares Hedge Replication ETF
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SPDR S&P 1500 Value Tilt ETF
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iShares Core S&P Total U.S. Stock Market ETF
ITOT
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SPDR Portfolio MSCI Global Stock Market ETF
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Schwab U.S. Broad Market ETF
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Dimensional U.S. Equity ETF
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